Category: mucopolysaccharidosis
VIMIZIM 1MG/ML SOL INJ FL 5ML (Elosulfase Alfa)
VIMIZIM 1MG/ML SOL INJ FL 5ML (Elosulfase Alfa) - Médicament désigné comme "orphelin" Treatment o
View DetailsNAGLAZYME 1 MG/ML PERF FL 5 ML (Galsulfase)
NAGLAZYME 1 MG/ML PERF FL 5 ML (Galsulfase) - Maladie rare sans désignation orpheline Long-term e
View DetailsELAPRASE 2 MG/ML PERF FL 3 ML (Idursulfase)
ELAPRASE 2 MG/ML PERF FL 3 ML (Idursulfase) - Médicament désigné comme "orphelin" Long-term treat
View DetailsALDURAZYME 100 U/ML INJ FL (Laronidase)
ALDURAZYME 100 U/ML INJ FL (Laronidase) - Maladie rare sans désignation orpheline Long-term enzym
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