CEREZYME 400 U INJ FL
(Imiglucerase) - Maladie rare sans désignation orpheline
Long-term enzyme replacement therapy in patients with a confirmed diagnosis of nonneuronopathic (Type 1) or chronic neuronopathic (Type 3) Gaucher disease and who exhibit clinically significant.
The non-neurological manifestations of Gaucher disease include one or more of the following conditions:
- Anaemia after exclusion of other causes, such as iron deficiency
- Thrombocytopenia
- Bone disease after exclusion of other causes such as Vitamin D deficiency
- Hepatomegaly or splenomegaly